Congrats to the team @pfizer for FDA approval of #AAV #GeneTherapy Beqvez for Hemophilia B 🎉 investors.pfizer.com/Investors/News…
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@Nicole_Paulk @pfizer Their vector AAV-Spark100 is supposed to be engineered to go to the liver. I don’t know how different their AAV is from naturally occurring AAVs, but it seems to me that engineered AAVs are going to be preferred for treatment of a whole slew of diseases.