The Heier Laboratory @TheHeierLab
Researching next generation treatments and biomarkers for pediatric diseases heierlab.org Washington, DC Joined September 2020-
Tweets40
-
Followers147
-
Following367
-
Likes125
We're hiring! We are excited to be in our new home @VCU in Richmond, VA and are actively recruiting lab members at all levels! If you're interested in basic or translational science in dystrophic muscle 💪 or heart ❤️, contact us!
Happy to share our latest article: Deletion of miR-146a enhances therapeutic protein restoration in model of dystrophin exon skipping: Molecular Therapy - Nucleic Acids cell.com/molecular-ther…. Congrats to first author and talented post-doc @nikkimmccormack! #DMD #microRNA (1/3)
The recent @FDA approval of the #MDA-Supported Drug AGAMREE® (vamorolone) from @CatalystForRare is a beacon of hope for people living with #Duchenne #MuscularDystrophy (#DMD), a rare but serious degenerative muscle disease. Learn more in #Quest: mdaquest.org/agamree-vamoro…
“CureDuchenne is proud to have contributed to the early development of vamorolone at ReveraGen." cureduchenne.org/general/fda-ap…
Today, the U.S. Food and Drug Administration (FDA) has granted its approval for Vamorolone, a new treatment for Duchenne Muscular Dystrophy (DMD) aged 2 years and older. worldduchenne.org/news/fda-appro…
Positive news for boys with #Becker #MuscularDystrophy: Vamorolone improves disease progression with fewer side effects than current treatments. Read more from @TheHeierLab, @AlysonAFiorillo & the Center for Genetic Medicine Research. ⬇️ …ovationdistrict.childrensnational.org/new-becker-mus…
Our new paper is out! Vamorolone improves disease and increases dystrophin in our Becker muscular dystrophy model. Now in clinical trials (NCT05166109) #MuscularDystrophy #Becker #dystrophin @FiorilloLab @MDAorg @ParentProjectMD @nih_nhlbi @iScience_CP cell.com/iscience/fullt…
Pleased to announce that the PDF file of our article on DG9-conjugated #morpholino and rescue in #SMA mice is now available @JCI_insight. This promising delivery strategy reached the CNS via an SC administration. insight.jci.org/articles/view/… @UAlberta_FoMD supported by @WCHRIUofA
Happy to share out latest methods paper on: Comprehensive Analyses of Muscle Function, Lean and Muscle Mass, and Myofiber Typing in Mice bio-protocol.org/en/bpdetail?id…
Thrilled to share our latest findings on the potential of DG9-conjugated morpholino as a treatment for spinal muscular atrophy! Our study shows significant improvements in survival, SMN expression, and muscle function in a mouse model. @UAlberta_FoMD insight.jci.org/articles/view/…
Pop Quiz!
Investigators at the Center for Genetic Medicine Research @AlysonAFiorillo & @MacGyver0282 created a model to test new treatments for Becker muscular dystrophy, providing hope to the growing number of patients with this debilitating neuromuscular disease. spr.ly/60173pSMX
I am so excited to share our newly published work on generating and characterizing the first mouse model of #Beckermusculardystrophy @MacGyver0282 @TheHeierLab @nikkimmccormack @EdgewiseTx @FiorilloLab #duchennemusculardystrophy #dystrophin doi.org/10.1002/jcsm.1…
1st mouse model of Becker muscular dystrophy!! Excited our bmx paper came out this week, check it out here: #Beckermusculardystrophy @AlysonAFiorillo @FiorilloLab @nikkimmccormack @EdgewiseTx @MDAorg @CureBMD @MDUK_News @ParentProjectMD #dystrophin onlinelibrary.wiley.com/doi/10.1002/jc…
If @NIHFunding raised the modular budget cap, what should it be raised to?
Only two weeks (and two days) to our first Circadian Biology Workshop at Cincinnati Children's - University of Cincinnati. Looking forward to new data, exciting new ideas and new collaborations in the making @CincyChildrens @CincyKidsOAACD @uofcincy
A huge round of applause 👏🏽 for the newly-minted Dr. Kelly Murphy, who has defended her dissertation investigating antisense oligonucleotide (AON) therapy for facioscapulohumeral #MuscularDystrophy (FSHD) in the Chen lab! 🎉💪🏽 #GWIBSFamily #DissertationProps #WomenInSTEM #PhDLife
Our lab is hiring postdocs to study muscle and heart function and disease through the perspectives of circadian, metabolic and epigenetic mechanisms. Our lab is committed to diversity, equity and inclusion and supports all career aspirations @CCHMCPostdoc
Irgueeubui @Irgueeubui4489
33 Followers 1K Following
Kelli @kellihayes70
184 Followers 3K Following
SabinaWillard @U2j5GgG088y7Lhm
68 Followers 7K Following
Znger @Znger4
491 Followers 5K Following Dream works believer. mAbs,CAR T, 😊NIK in NFkB pathway-G-proteins-,Chl Binding Proteins, DmNucleobindin-Microb Diversity-Reduviids
Ildernandes Vieira-Al... @ildernandes
84 Followers 400 Following Vascular Physiology, PhD⚗️🧑🔬 I'm trying to understand how life works - Universidade Federal de Minas Gerais, Belo Horizonte, Brazil
Namita Patel @namitapatelmd
568 Followers 1K Following PGY3 @URMC_Neurology. MD @VCU'22. @UofT'16. #ClinicalResearch #MedEd #Advocacy. Outdoor Enthusiast. Views my own.
CarolineMinnie @CwT978k5P3E0c8e
69 Followers 7K Following
Ling Wang @LWang_UIowa
255 Followers 510 Following Biomedical researcher, mom of two daughters. Vascular and redox biology, nitrite-NO signaling, skeletal muscle.
Hongshuai Li Lab @LiMgrl_Uiowa
181 Followers 410 Following Focus on musculoskeletal growth and regeneration. Muscular dystrophy, Muscle/bone crosstalk, Stem cells. Department of Orthopedics and Rehabilitation, UIowa.
@fightingforcharlie @DMDCharlie
280 Followers 5K Following Duchenne Muscular Dystrophy Awareness (Dad to Charlie Henrik) DMD Advocate & caregiver : https://t.co/1qeTGpxpOw.
Tought @Tought180626
78 Followers 5K Following
Billy Valentine @wmjvalentine1
8 Followers 104 Following
@MyBeckersStory | Dis... @MyBeckersStory
2K Followers 2K Following “The BMD Blogger” Exploring life with Becker Muscular Dystrophy - the victories, the defeats, and everything in between! Book Available ⤵️
CureCalpain3 @CureCalpain3
340 Followers 154 Following C3 is a non-profit organization driving research to cure limb-girdle muscular dystrophy type 2A, also referred to as LGMD2A/R1 and Calpainopathy
Colin Werth @cjwerth10
70 Followers 403 Following
Padashi @Padashi478983
39 Followers 1K Following
DIYAR BARKAL @Diyar_barkal22
8 Followers 39 Following Becker muscular dystrophy From: syria 22years old whatsapp : +963992029169
Matti Allen @Matti_D_Allen
100 Followers 480 Following Neuromuscular Medicine Fellow (2023-2024) at The Ohio State University; MD Queen's University; PhD The University of Western Ontario
Diyar Barkal @diyar_barkal
1 Followers 20 Following
Lil_Jean @LilJeanGrey
620 Followers 2K Following Survived PhD school @UF_HHP. Embracing PDF @IUICMH 🇲🇾
Kathryn Fair @KathrynFair4
0 Followers 11 Following
Christopher Perry PhD @ChrisPerryMito
3K Followers 971 Following Researcher/educator of muscle disorders and the metabolic basis of muscle fitness. Translating mitochondrial bioenergetics and redox biology to health/disease.
Aurora Scientific @AuroraSci
825 Followers 776 Following Muscle physiology and Neuroscience systems and solutions. Follow us for news, useful tips and updates on the fields of muscle physiology and neuroscience.
Ashoqullah Haqyar @AshoqullahHaqy4
73 Followers 576 Following زه د BMD ناروغ يم تاسو راسره د دې ناروغۍ په علاج کې څه مرسته کولى شئ واټس آپ 0785192021
Kathryn J. Swoboda @kswobo
240 Followers 252 Following Neurologist, Geneticist, Neurophysiologist on break. Views expressed are my own.
Marine Theret, 🇫�... @marine_theret
904 Followers 1K Following Ph.D - RA in Fabio Rossi lab @sbme_ubc |she, her, hers| Working on #MSC #inflammation #fibrosis |
William-Jose Velez Go... @williamjose
909 Followers 5K Following Account dormant because of the psychopath who owns the site. You can connect at https://t.co/4jRTMliGrP
Quantabio @Quanta_bio
335 Followers 2K Following #Quanta_bio is a leader in PCR, qPCR, NGS and cDNA synthesis reagents that support applied, translation and life science research #PCR #NGS #lifescience
Chris Rand @ChrisRand22
364 Followers 643 Following Dad. Husband. Diehard Leafs Fan. Supporting Scientific Discovery with Aurora Scientific. Jack of all trades, master of pun. Tweets are my own.
Andrea Pereyra, MD/Ph... @ASPereyra
681 Followers 1K Following Assistant Director, Postdoc Life Design @JohnsHoopkins/ Advocating for happy careers and amazing futures / Scientist Forever / BoD @nationalpostdoc
Katie Shrader @KatieAShrader
147 Followers 1K Following Strategic communicator. Wordsmith. Inclusion advocate. @UVA & @AP alum. Passion: healthcare for kids. Views: mine.
Gordon Lynch @GordonSLynch
3K Followers 1K Following Professor of Physiology @unimelb PhD FACSM CSCS Passionate researcher & mentor in muscle biology. Health presenter on Australia's ABC Radio @abcovernights
Kerry Spink @KerrySpink
403 Followers 1K Following Trusts Fundraising Manager/SEN parent/ FSH muscular dystrophy advocate/ dog walks, great books & a brew. All views are my own
Abigail Mackey @AbigailMackey1
4K Followers 2K Following @abigailmackey1.bsky.social | Clinical Professor of Muscle Physiology and Regeneration @ISMCopenhagen | https://t.co/dFON0ibygG
Lesley - FPL ⚽️�... @Weggster
8K Followers 6K Following Blocked by FessHole. JK Rowling once liked my Tweet. My laugh triggers fire alarms. Music & Gig junkie.Incompetent Fantasy Football Manager. Potty mouth. #FPL
Saifullah Saifullah, ... @saifullahjstu2
6 Followers 22 Following Lecturer, Dept. of Genetic Engineering & Biotechnology, Jashore University of Science & Technology (JUST), Bangladesh. Research Focus on Gene Therapy.
LitMetric @LitMetric
810 Followers 268 Following Explore Scientific Literature Easily find the world's top scientific articles and authors
BC @Blamont12B
323 Followers 3K Following
Vitor Lira @VitorALira
201 Followers 242 Following Health & Human Physiology Associate Professor at the University of Iowa studying how protein recycling preserves muscle force and metabolism as we age.
Jyoti K Jaiswal @jyoti_k_jaiswal
364 Followers 176 Following Cell biologist studying cell injury, infection, and muscle repair; Professor, George Washington University and Children’s National Hospital
Bill Quirk @Quirk2011
144 Followers 220 Following Petworth Dad, attorney & Director of Government Relations and Public Affairs for Valley Health.
MangoStreetDC @MangoStreet_DC
33 Followers 161 Following
DMM Journal @DMM_Journal
3K Followers 631 Following Disease Models & Mechanisms - discovery for human health. A @Co_Biologists Open Access journal that publishes human disease research.
VCU Neurology & Neuro... @VCUNeuro
1K Followers 97 Following Official Twitter/X account for the Departments of Neurology and Neurosurgery, and Residency Program at VCU.
VCU @VCU
69K Followers 10K Following We do things differently at Virginia Commonwealth University because we know different works. Unconventional minds welcome. #UncommonVCU
VCU News Center @VCUnews
21K Followers 967 Following Virginia Commonwealth University (@VCU) news and media coverage, by VCU Public Relations. For media inquiries, contact us at https://t.co/Zj27TINZf8
A. Gordon Smith, MD @gordonsmithMD
453 Followers 95 Following Chair of Neurology at Virginia Commonwealth University (@VCUHealth).
Children's Hospital o... @childrensatvcu
5K Followers 2K Following From casts to cancer – from simple to complex – we do everything in our power to give kids the best shot at a healthy future.
Eric T Wang @EricTWang
1K Followers 722 Following
Nicholas Johnson @nickjohnson30
351 Followers 46 Following Neurologist, vice chair of research, neuromuscular specialist at Virginia Commonwealth University
Jesse Damsker @JesseDamsker
18 Followers 42 Following Born and raised in Philadelphia. Now a senior research scientist at ReveraGen Biopharma and Assistant Research Professor at Children's National Medical Center.
CureCalpain3 @CureCalpain3
340 Followers 154 Following C3 is a non-profit organization driving research to cure limb-girdle muscular dystrophy type 2A, also referred to as LGMD2A/R1 and Calpainopathy
Nikki McCormack @nikkimmccormack
43 Followers 39 Following
MangoStreetDC @MangoStreet_DC
33 Followers 161 Following
Kathryn J. Swoboda @kswobo
240 Followers 252 Following Neurologist, Geneticist, Neurophysiologist on break. Views expressed are my own.
UMR LBEPS @UMR_LBEPS
202 Followers 178 Following Laboratoire de Biologie de l'Exercice pour la Performance et la Santé (LBEPS) 🇫🇷 Exercise Physiology & Biology Lab at 🧡💙@UnivEvry - @UnivParisSaclay💜🤍
Christopher Perry PhD @ChrisPerryMito
3K Followers 971 Following Researcher/educator of muscle disorders and the metabolic basis of muscle fitness. Translating mitochondrial bioenergetics and redox biology to health/disease.
Chris Rand @ChrisRand22
364 Followers 643 Following Dad. Husband. Diehard Leafs Fan. Supporting Scientific Discovery with Aurora Scientific. Jack of all trades, master of pun. Tweets are my own.
Katie Shrader @KatieAShrader
147 Followers 1K Following Strategic communicator. Wordsmith. Inclusion advocate. @UVA & @AP alum. Passion: healthcare for kids. Views: mine.
Matthias Lambert, PhD @MatthiasLambert
736 Followers 701 Following Muscle Biologist | Rare Diseases Expert | Patient-Scientist 🇫🇷🇺🇲 Past @univ_lille, @harvardmed, @BostonChildrens, & Kunkel lab team member
Halli @iamharaldur
269K Followers 20 Following Tweets auto delete. Founder @uenodotco and Anna Jóna. Building wheelchair ramps @rampupteam. Chairman @hafnarhaus. Music @onnujonuson. Host Let's Walk podcast.
FiorilloLab @FiorilloLab
42 Followers 104 Following Principal Investigator at Children's National Medical Center. Our lab focuses on dysregulated miRNAs in DMD and other muscle disorders.
William-Jose Velez Go... @williamjose
909 Followers 5K Following Account dormant because of the psychopath who owns the site. You can connect at https://t.co/4jRTMliGrP
Keitaro Yamanouchi, P... @ArtisanKeitaro
280 Followers 913 Following 東京大学大学院農学生命科学研究科獣医生理学教室教授（2022.4.1付）。釣りネタが多いです。職業柄、非科学的、非論理的で無責任な言動は許せません。日本をまともな国家に。ツイートは個人の意見に基づくものです。ラボのHPはこちら→https://t.co/JK9AtGTQPi
Bad Lip Reading @BadLipReading
294K Followers 103 Following I put words into other people's mouths. The OFFICIAL Bad Lip Reading Twitter account
DC Soccer Club @DCSoccerClub
2K Followers 387 Following DC Soccer Club is a youth soccer organization, providing organized teams and supervised games for players between pre-k and college. https://t.co/Q7sanvcFHa
Michelle Beadle @MichelleDBeadle
1.3M Followers 4K Following I like barefoot walks on gravel roads. Staring at spots on a wall. Awkward silences. And dogs. Oh…and I sometimes talk about sports.
💀 @CDCarter13
53K Followers 2K Following
SaveMacGyverHQ @SaveMacGyverHQ
838 Followers 60 Following **Inactive account.** A group of MacGyver (2016) fans who believe the show should be saved for Season 6! #SaveMacGyver 🖇
Dr Kareem Carr, Stati... @kareem_carr
172K Followers 350 Following Statistician. PhD @Harvard • Follow me for fun, nerdy content • Author of the Vital Statistics newsletter (link in bio)
Dr Ellie Murray, ScD @EpiEllie
123K Followers 2K Following Epidemiologist and science communicator | cohost @casualinfer podcast | Newsletter: E is for Epi at https://t.co/xvuWpBQ4tN
Joe Gould @reporterjoe
15K Followers 6K Following @Politico defense reporter. DMs open. Signal: reporterjoe.01 Ex @Defense_News, @ArmyTimes, @NYDailyNews. BK native.
Crown Valley Imaging @crown_valley
10K Followers 11K Following Crown Valley Imaging is a diagnostic imaging facility that offers exceptional patient care. We offer MRI, CT-Scan, X-Ray, DEXA and Ultrasound
Anna Luiza @sma_anna2019
418 Followers 2K Following Official intl profile of @ame_anna2019 👧🏻 SMA1 fighter 🎂2 years old 💉 My life DEPENDS on Zolgensma! 🧬 To help Anna ⬇️ https://t.co/Txwu5yVSfj
Personalised Medicine... @PersonalMedNI
2K Followers 2K Following School of Medicine, Ulster University #research | #education | #innovation #precisionmedicine #genomics #personalisedmedicine #pharmacogenomics #health
RARE Revolution Magaz... @RareRevolutionM
12K Followers 7K Following Digital magazine giving a voice to those affected by rare conditions and the charities that support them. Contact us: [email protected]
Taben M. Hale, PhD @TMHalePhD
2K Followers 2K Following #Cardiovascular #pharmacologist #physiologist researching #fibrosis #hypertension #DOHAD #autonomic regulation 🇨🇦
Pilar Alcaide, PhD @PilarAlcaidePhD
3K Followers 833 Following Cardiovascular Immunologist. Professor at the University of Miami. Always with the goal ⚽️ in mind. S is for ⚽️ ⛷ and SCIENCE.
Prof. Karen Anthony @Weekademia
794 Followers 1K Following Professor of Molecular Medicine @UniNorthants researching neurodegenerative & neuromuscular disorders. I like RNA. 🔬
Sean M Wu, MD PhD @SeanM_Wu
7K Followers 5K Following Stanford Professor of Medicine/Cardiology, Sr. Vice Chair Academic Affairs, Dept of Med, Investigator in Cardiac Development, Regenerative Med & Bioengineering.
Mary @Marypu91
33 Followers 164 Following Hoping one day SMA would be just part of our past. #curetype3too
Joseph W. Franses MD-... @JosephFranses
92 Followers 259 Following Physician-scientist in GI oncology at @UCCancerCenter, husband and father
Campbell Muscle Lab @... @CampbellLabatUK
945 Followers 1K Following Pushing back the boundaries of translational research at University of Kentucky: heart failure, contractility, sarcomeres, mathematical modeling, biobanking.
Centre for Muscle Res... @UniMelbCMR
3K Followers 1K Following Advancing muscle biology and its importance in health and disease. #myotwitter #sarcopenia #myology #skeletalmuscle #musculoskeletal #neuromuscular #cachexia
Christopher Toepfer @ChrisToepfer
1K Followers 1K Following Associate Professor of Cardiovascular Science @UniofOxford. Researching Inherited & acquired heart disease.
Khrystal K. Davis, JD @KhrystalKDavis
19K Followers 18K Following Founder @txrare Dedicated to Improving Access for the Rare Disease Community. Hunter’s (SMA Type 1) Zebra Mom 🦓. Patient Advocate. Speaker. Author. 👦 🧬🦓
Martin Frank @FranklyPhysiol
2K Followers 1K Following Retired American Physiological Society Executive Director,. Tweets are my opinions. RTs are not necessarily endorsements!
Jon D. Moulton @jonmoulton
1K Followers 2K Following Curating Morpholino oligo citations. Work@Gene Tools, LLC: biology, chemistry, antisense. Also: environ science, China, veggie gardening.Trends for United States
You might like
