n-Lorem Foundation @n_lorem
Non-profit discovering, developing, and providing personalized experimental ASO medicines to treat nano-rare patients — for free, for life nlorem.org Carlsbad, CA Joined July 2020-
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The countdown is on! Just 50 days until the #NRPC25! We can’t wait to bring the community together. nlorem.org/nano-rare-pati…
Research, published in Nucleic Acids Research, identifies splice-modulating ASO that corrects the effects of a nano-rare GBE1 indel mutation, offering a potential path to treatment for a subset of APBD nano-rare patients. Read: nlorem.org/n-lorem-founda…
📢 We’re excited to announce that Elizabeth Berry-Kravis, MD, PhD, of @RushUniversity Medical Center, will be joining us at #NRPC25! Event details: nlorem.org/nano-rare-pati…
Olivia Kim-McManus, MD, of @radychildrens and @UCSDHealth will be joining us at the #NRPC25 Register to attend in person or virtually: nlorem.org/nano-rare-pati…
Spine Enthusiast, a distributor of spinal implants, allografts and biologics supporting surgical cases ranging from outpatient procedures to complex deformity corrections for adolescents and adults, joins us in support of the #NRPC25 👏 nlorem.org/nano-rare-pati…
The nano-rare community is gathering for the #NRPC25. Don’t miss it! Join us for this free event in Boston on October 20-21. nlorem.org/nano-rare-pati…
WATCH: Hope for Kinsley: Facing TUBB4A with Courage and Care youtu.be/omlkQPRVWzU
Our trusted partner providing n-Lorem with toxicology services, Charles River rejoins us as a sponsor of the 2025 Nano-rare Patient Colloquium. @CRiverLabs Learn more about the #NRPC25: nlorem.org/nano-rare-pati…
Today, we celebrate RNA Day! It's a perfect moment to recognize the molecule at the heart of our mission. From design to discovery to development, RNA is central to everything we do at n-Lorem as we work to deliver hope and personalized ASOs to patients in need.
🎙️ n-Lorem Founder, Stan Crooke, joined #BiomedicalFrontiers to talk about #Antisense, nano-rare diseases, and why, instead of retiring, he chose to build n-Lorem—creating personalized ASO medicines for patients no one else could help. Listen: rss.com/podcasts/biome…
Alnylam Pharmaceuticals, the leading RNAi therapeutics company, rejoins us as a sponsor of the 2025 Nano-rare Patient Colloquium. Thank you, @Alnylam, for your continued support and commitment to nano-rare patients! #NRPC25 info: nlorem.org/nano-rare-pati…
As a non-profit, we discover, develop, and provide personalized experimental ASO medicines to treat children and adults living with nano-rare diseases. Be part of something extraordinary. nlorem.org/donate/
Parexel, a leading global clinical research organization, rejoins us as a sponsor of the #NRPC25. Thank you for collaborating with heart through your continued support of n-Lorem and the nano-rare community! Discover more: nlorem.org/nano-rare-pati…
Great to be at the inaugural ReNU Hope Conference and Scientific Symposium! n-Lorem featured two presentations and a scientific poster highlighting our ReNU research efforts.

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