Amicus Therapeutics @amicusrx1
We are a global biotech company focused on discovering, developing & delivering high-quality medicines for people living with rare diseases. amicusrx.com Princeton, NJ Joined October 2014-
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Thanks to everyone who joined our #NHSConfedExpo poll! The correct answer was C. People living with a rare disease. 1 in 17 people in the UK live with a rare condition. We must continue to listen, learn, and take action to address the health inequities they face.
Thanks to everyone who joined our #NHSConfedExpo poll! The correct answer was C. People living with a rare disease. 1 in 17 people in the UK live with a rare condition. We must continue to listen, learn, and take action to address the health inequities they face.
Our team made a strong impact at #NHSConfedExpo, with sessions focused on addressing the health inequalities faced by the #RareDisease community. Thanks to our speakers and all who joined us, visited our stand, and contributed to our live mural. #ClosingTheCareGap #AmicusCares
To coincide with our presence at #NHSConfedExpo, we'd love your input on this: Of the following groups, which do you think there are more of living in the UK? NP-NN-ALL-00100525 | May 2025
We’re heading to #NHSConfedExpo in Manchester UK! Catch our two sessions on closing the care gap in rare diseases and visit our stand to help create a live mural highlighting health inequality. Look forward to seeing you there! #AmicusTherapeutics #ClosingTheCareGap #AmicusCares
We are thrilled to announce the expansion of our pipeline with the U.S. licensing of DMX-200 to bring even more hope to people living with rare diseases. Read more here: ir.amicusrx.com
The journey to a #Fabry disease diagnosis can be long and complex. Watch Dr James O’Donovan sit down with Loretta MacInnes to discuss the challenges of diagnosis. Full video: youtu.be/VeFTBHSiMJU?fe…… #amicuscares #CouldItBeFabryNP- NN-IN-00010325
With the vital help of our patient community partners, we are thrilled to see our study published emphasizing the importance of understanding the quality of life and lived experiences of those with late-onset Pompe disease (#LOPD). bit.ly/3R0g18W
We’re presenting our Q4 and Full Year 2024 results today at 8.30am ET on a live audio webcast with our President and Chief Executive Officer Bradley Campbell. Find out more here: tinyurl.com/4hnskbp2 #Earnings #AmicusTherapeutics
We are excited to join with the lysosomal diseases community at this year’s @worldsymposium . Together, we’ve made remarkable progress in the fight against rare diseases. And together, we can do even more. Patients are counting on us -- all of us. #WORLDSymposia #RareDiseases
Today the UK based Office of Health Economics (OHE) has published a report, funded by Amicus, on the need for supplier diversity in rare disease markets.
Today the UK based Office of Health Economics (OHE) has published a report, funded by Amicus, on the need for supplier diversity in rare disease markets.
#JPM25 has been a great opportunity to connect with others in the industry to see what difference we can make for patients, performance, and partnering. Missed our live webcast updating on our successes from 2024? Listen via the following link: bit.ly/429Mz7v
In November, Team Amicus took on the Rocky Run half marathon to raise awareness and funds for @wishnj. Together with Fight Like Frankie, we had the honor of visiting the Make-A-Wish Castle to present our donation- a testament to the power of community and commitment! #AmicusCares
We’re presenting today at #JPM25 at 3pm PT / 6pm ET. Follow the link below for the live audio webcast with our President and Chief Executive Officer Bradley Campbell. ir.amicusrx.com/events/event-d…
At #JPM25 today, Amicus President and Chief Executive Officer Bradley Campbell will highlight our accomplishments in 2024 and share what’s ahead for our company in 2025. Learn more here: ir.amicusrx.com/news-releases/…
Today we announced our preliminary full-year 2024 results and what’s ahead for our company in 2025. Learn more here: ir.amicusrx.com/news-releases/…
As we welcome 2025, we remain steadfast in our commitment to improving the lives of people living with #rarediseases. Here’s to a year filled with hope, collaboration, and advancements for the rare disease community. #HappyNewYear from everyone at Team Amicus! #AmicusCares
Amicus Therapeutics will be participating in the 43rd Annual J.P. Morgan Healthcare Conference. Join us for a presentation delivered by Bradley Campbell, President and Chief Executive Officer on Monday, January 13, 2025, at 3:00 p.m. PT tinyurl.com/2p8x8zx6 #JPM25
From all of us at Amicus, we wish you and your loved ones a joyful holiday season and a hopeful, healthy new year! #HappyHolidays #RareDisease #AmicusCares
This International Day of Persons with Disabilities, we commend the contributions of people with disabilities in shaping a more inclusive future. We see their strength in the rare disease community and recognize the positive impact greater inclusion can have. #AmicusCares #IDPD
We are thankful for the strength and resilience of patients, families, and caregivers in the rare disease community, including our dedicated employees, partners, and supporters committed to making a difference. Happy Thanksgiving from Team Amicus! #Thanksgiving #AmicusCares

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